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Retinal disorders v8.124 AP5B1 Ida Ertmanska changed review comment from: 2 unrelated cases reported in PMID: 40081374 - see review by Sarah Leigh.

New cases:
PMID: 41830174 Hussian et al., 2026
2 unrelated European families reported with biallelic AP5B1 variants and AP5B1-related retinopathy.
Family 4: female proband, homozygous for AP5B1: c. 2354T>C, p.Leu785Pro. Diagnosed with retinal dystrophy at age 33yrs.
Family 5: female proband, age 44yrs (disease onset at 39yrs), with compound het AP5B1 variants: c. 2354T>C, p.Leu785Pro & c.188delA, p.Gln63Argfs*95.

This gene is not yet associated with a phenotype in OMIM (accessed 15th Apr 2026).; to: 2 unrelated cases reported in PMID: 40081374 - see review by Sarah Leigh.

New cases:
PMID: 41830174 Hussain et al., 2026
2 unrelated European families reported with biallelic AP5B1 variants and AP5B1-related retinopathy.
Family 4: female proband, homozygous for AP5B1: c. 2354T>C, p.Leu785Pro. Diagnosed with retinal dystrophy at age 33yrs.
Family 5: female proband, age 44yrs (disease onset at 39yrs), with compound het AP5B1 variants: c. 2354T>C, p.Leu785Pro & c.188delA, p.Gln63Argfs*95.

This gene is not yet associated with a phenotype in OMIM (accessed 15th Apr 2026).
Retinal disorders v8.123 AP5B1 Ida Ertmanska Publications for gene: AP5B1 were set to 40081374
Retinal disorders v8.122 AP5B1 Ida Ertmanska Phenotypes for gene: AP5B1 were changed from Lysosomal macular dystrophy to macular dystrophy, retinal, MONDO:0031166
Retinal disorders v8.121 AP5B1 Ida Ertmanska Classified gene: AP5B1 as Amber List (moderate evidence)
Retinal disorders v8.121 AP5B1 Ida Ertmanska Added comment: Comment on list classification: There are now 4 unrelated cases with biallelic AP5B1 variants and retinal disease. Hence, this gene can be promoted to Green at the next update, with MOI set to BIALLELIC, autosomal or pseudoautosomal.
Retinal disorders v8.121 AP5B1 Ida Ertmanska Gene: ap5b1 has been classified as Amber List (Moderate Evidence).
Retinal disorders v8.120 AP5B1 Ida Ertmanska Tag Q2_26_promote_green tag was added to gene: AP5B1.
Retinal disorders v8.120 AP5B1 Ida Ertmanska reviewed gene: AP5B1: Rating: GREEN; Mode of pathogenicity: None; Publications: 40081374, 41830174; Phenotypes: macular dystrophy, retinal, MONDO:0031166; Mode of inheritance: BIALLELIC, autosomal or pseudoautosomal
Retinal disorders v7.19 AP5B1 Sarah Leigh Phenotypes for gene: AP5B1 were changed from Macular dystrophy to Lysosomal macular dystrophy
Retinal disorders v7.18 AP5B1 Sarah Leigh Publications for gene: AP5B1 were set to PMID 40081374
Retinal disorders v7.17 AP5B1 Sarah Leigh Classified gene: AP5B1 as Amber List (moderate evidence)
Retinal disorders v7.17 AP5B1 Sarah Leigh Gene: ap5b1 has been classified as Amber List (Moderate Evidence).
Retinal disorders v7.16 AP5B1 Sarah Leigh reviewed gene: AP5B1: Rating: AMBER; Mode of pathogenicity: None; Publications: ; Phenotypes: ; Mode of inheritance: None
Retinal disorders v7.13 AP5Z1 Sarah Leigh changed review comment from: In PMID: 40081374, Kaminska et al report variants in three of the genes which encode different subunits of the vesicular fifth adaptor protein (AP-5) complex: AP5Z1, AP5M1, and AP5B1, in patients with a specific form of macular degeneration. Seventeen biallelic AP5Z1 variants were been reported in fourteen unrelated families with macular degeneration. Due to the involvement of variants in the AP-5 complex, the authors suggest that the resultant condition should be called lysosomal macular dystrophy.; to: In PMID: 40081374, Kaminska et al report variants in three of the genes which encode different subunits of the vesicular fifth adaptor protein (AP-5) complex: AP5Z1, AP5M1, and AP5B1, in patients with a specific form of macular degeneration. Seventeen biallelic AP5Z1 variants were been reported in fourteen unrelated families, three homozygous AP5M1 variant were found in three unrelated cases and three biallelic AP5B1 variants were found in two unrelated cases. Due to the involvement of variants in the AP-5 complex, the authors suggest that the resultant condition should be called lysosomal macular dystrophy.
Retinal disorders v7.8 AP5B1 Siying Lin gene: AP5B1 was added
gene: AP5B1 was added to Retinal disorders. Sources: Literature
Mode of inheritance for gene: AP5B1 was set to BIALLELIC, autosomal or pseudoautosomal
Publications for gene: AP5B1 were set to PMID 40081374
Phenotypes for gene: AP5B1 were set to Macular dystrophy
Mode of pathogenicity for gene: AP5B1 was set to Other
Review for gene: AP5B1 was set to GREEN
Added comment: 2 individuals from 2 families with biallelic loss of function variants and macular dystrophy
Sources: Literature