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Hereditary ataxia v1.337 NUS1 Achchuthan Shanmugasundram Classified gene: NUS1 as Green List (high evidence)
Hereditary ataxia v1.337 NUS1 Achchuthan Shanmugasundram Added comment: Comment on list classification: As reviewed by Dmitrijs Rots, there is sufficient evidence available (~10 unrelated patients and functional evidence) for the promotion of this gene to green rating.
Hereditary ataxia v1.337 NUS1 Achchuthan Shanmugasundram Gene: nus1 has been classified as Green List (High Evidence).
Hereditary ataxia v1.336 NUS1 Achchuthan Shanmugasundram Phenotypes for gene: NUS1 were changed from intellectual disability; seizures; ataxia; dystonia; tremor to hereditary ataxia, MONDO:0100309
Hereditary ataxia v1.335 NUS1 Achchuthan Shanmugasundram Publications for gene: NUS1 were set to 33731878; 32334381; 32485575; 31656175
Hereditary ataxia v1.334 NUS1 Achchuthan Shanmugasundram reviewed gene: NUS1: Rating: GREEN; Mode of pathogenicity: None; Publications: 31656175, 32485575, 32959737, 33731878, 38291835; Phenotypes: hereditary ataxia, MONDO:0100309; Mode of inheritance: MONOALLELIC, autosomal or pseudoautosomal, NOT imprinted
Hereditary ataxia v1.228 NUS1 Dmitrijs Rots gene: NUS1 was added
gene: NUS1 was added to Hereditary ataxia. Sources: Literature
Mode of inheritance for gene: NUS1 was set to MONOALLELIC, autosomal or pseudoautosomal, NOT imprinted
Publications for gene: NUS1 were set to 33731878; 32334381; 32485575; 31656175
Phenotypes for gene: NUS1 were set to intellectual disability; seizures; ataxia; dystonia; tremor
Penetrance for gene: NUS1 were set to Complete
Review for gene: NUS1 was set to GREEN
Added comment: Multiple patients (see below) with de novo or heterozygous variants reported. The phenotype include ID, seizures and/or movement disorder (including tremor, ataxia, dystonia). Functional analysis of patients fibroblasts shows"de novo NUS1 variants reduce NgBR and Niemann–Pick type C2 (NPC2) protein amount, impair dolichol biosynthesis, and cause lysosomal cholesterol accumulation." (Yu et al,m 2021). Movement abnormalities and similar metabolic dysfunction in zebrafish model.

3 patients with ataxia reported in: PMID: 33731878
One patient with dystonia reported in: PMID: 32334381
One family with ataxia reported in: PMID: 32485575
Two cases with ataxia reported in: PMID: 31656175

Additionally, two cases from one family with homozygous missense variant, but NO ataxia is reported:PMID: 25066056
Sources: Literature