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Congenital myopathy v6.43 RFC4 Achchuthan Shanmugasundram Tag Q3_24_promote_green was removed from gene: RFC4.
Congenital myopathy v6.43 RFC4 Achchuthan Shanmugasundram commented on gene: RFC4: The rating of this gene has been updated to green following NHS Genomic Medicine Service approval.
Congenital myopathy v6.42 RFC4 Achchuthan Shanmugasundram Source Expert Review Green was added to RFC4.
Source NHS GMS was added to RFC4.
Rating Changed from Amber List (moderate evidence) to Green List (high evidence)
Congenital myopathy v4.44 RFC4 Achchuthan Shanmugasundram Classified gene: RFC4 as Amber List (moderate evidence)
Congenital myopathy v4.44 RFC4 Achchuthan Shanmugasundram Added comment: Comment on list classification: There is sufficient evidence available for the association of this gene with congenital myopathy. Hence, this gene should be promoted to green rating in the next GMS update.
Congenital myopathy v4.44 RFC4 Achchuthan Shanmugasundram Gene: rfc4 has been classified as Amber List (Moderate Evidence).
Congenital myopathy v4.43 RFC4 Achchuthan Shanmugasundram Tag Q3_24_promote_green tag was added to gene: RFC4.
Congenital myopathy v4.43 RFC4 Achchuthan Shanmugasundram gene: RFC4 was added
gene: RFC4 was added to Congenital myopathy. Sources: Literature
Mode of inheritance for gene: RFC4 was set to BIALLELIC, autosomal or pseudoautosomal
Publications for gene: RFC4 were set to 39106866
Phenotypes for gene: RFC4 were set to congenital myopathy, MONDO:0019952
Review for gene: RFC4 was set to GREEN
Added comment: PMID:39106866 reported nine individuals (aged birth to 47 years) from eight unrelated families with a multisystem disorder.

They presented with muscle weakness/myopathy (9/9), motor incoordination/gait disturbance (8/8), delayed gross motor development (6/9), dysarthria (5/5), peripheral neuropathy (3/3 adults), bilateral sensorineural hearing impairment (6/9), decreased body weight (8/9), short stature (5/9), microcephaly (4/9), respiratory issues/insufficiency (6/9), cerebellar atrophy (4/9), pituitary hypoplasia (3/9).

The age of onset of eight of nine individuals ranged from neonatal to childhood, while one individual had onset of symptoms in mid-30s.

They were identified with biallelic loss-of-function variants in RFC4 gene (3 frameshift, 2 splice site, 1 single AA duplication, 2 single AA deletions and 2 missense)

This gene has not yet been associated with relevant phenotypes either in OMIM or in Gene2Phenotype.
Sources: Literature