Limb girdle muscular dystrophies, myofibrillar myopathies and distal myopathies

Gene: SNUPN

Green List (high evidence)

SNUPN (snurportin 1)
EnsemblGeneIds (GRCh38): ENSG00000169371
EnsemblGeneIds (GRCh37): ENSG00000169371
OMIM: 607902, Gene2Phenotype
SNUPN is in 3 panels

3 reviews

Arina Puzriakova (Genomics England Curator)

Green List (high evidence)

The rating of this gene has been updated to green following NHS Genomic Medicine Service approval.
Created: 11 Dec 2025, 10:47 a.m. | Last Modified: 11 Dec 2025, 10:47 a.m.
Panel Version: 5.24

Achchuthan Shanmugasundram (Genomics England Curator)

Green List (high evidence)

Comment on list classification: As reviewed by Dmitrijs Rots, there is sufficient evidence available for the promotion of this gene to green rating in the next GMS update.
Created: 26 Apr 2025, 4:58 p.m. | Last Modified: 26 Apr 2025, 4:58 p.m.
Panel Version: 4.45
PMID:38366623 reported five patients from two unrelated families with a limb-girdle muscular dystrophy (LGMD) phenotype characterised by early-onset proximal weakness, restrictive respiratory dysfunction and frequent contractures. They were identified with a homozygous variant in SNUPN gene (p.Ile309Ser). Functional studies available in patient-derived cells and muscle biopsies, and in vivo Drosophila model support that SNUPN variants are the cause of this LGMD phenotype.

PMID:38413582 reported 18 children from 15 unrelated families with muscular phenotypes, including proximal upper limb weakness, distal upper and lower limb weakness, and myopathy (EMG) with elevated serum creatinine kinase level. They were identified with nine different hypomorphic biallelic variants in the SNUPN gene, predominantly clustered in the last coding exon. Functional studies showed that SPN1 variant failed to oligomerize leading to cytoplasmic aggregation in patients’ primary fibroblasts.

This gene has already been associated with relevant phenotype in OMIM (MIM #620793).
Created: 26 Apr 2025, 4:56 p.m. | Last Modified: 26 Apr 2025, 4:56 p.m.
Panel Version: 4.42

Mode of inheritance
BIALLELIC, autosomal or pseudoautosomal

Phenotypes
Muscular dystrophy, limb-girdle, autosomal recessive 29, OMIM:620793

Publications

Dmitrijs Rots (Children's Clinical University Hospital)

Green List (high evidence)

The study reports:"18 children from 15 unrelated families who present with atypical muscular dystrophy and neurological defects"
Sources: Literature
Created: 24 Aug 2024, 1:28 p.m.

Mode of inheritance
BIALLELIC, autosomal or pseudoautosomal

Phenotypes
muscular dystrophy

Publications

Details

Mode of Inheritance
BIALLELIC, autosomal or pseudoautosomal
Sources
  • Expert Review Green
  • NHS GMS
Phenotypes
  • Muscular dystrophy, limb-girdle, autosomal recessive 29, OMIM:620793
OMIM
607902
Clinvar variants
Variants in SNUPN
Penetrance
None
Publications
Panels with this gene

History Filter Activity

11 Dec 2025, Gel status: 3

Removed Tag

Arina Puzriakova (Genomics England Curator)

Tag Q2_25_ promote_green was removed from gene: SNUPN.

11 Dec 2025, Gel status: 3

Added New Source, Added New Source, Status Update

Arina Puzriakova (Genomics England Curator)

Source NHS GMS was added to SNUPN. Source Expert Review Green was added to SNUPN. Rating Changed from Amber List (moderate evidence) to Green List (high evidence)

26 Apr 2025, Gel status: 2

Entity classified by Genomics England curator

Achchuthan Shanmugasundram (Genomics England Curator)

Gene: snupn has been classified as Amber List (Moderate Evidence).

26 Apr 2025, Gel status: 0

Set Phenotypes

Achchuthan Shanmugasundram (Genomics England Curator)

Phenotypes for gene: SNUPN were changed from muscular dystrophy to Muscular dystrophy, limb-girdle, autosomal recessive 29, OMIM:620793

26 Apr 2025, Gel status: 0

Set publications

Achchuthan Shanmugasundram (Genomics England Curator)

Publications for gene: SNUPN were set to 38413582

26 Apr 2025, Gel status: 0

Added Tag

Achchuthan Shanmugasundram (Genomics England Curator)

Tag Q2_25_ promote_green tag was added to gene: SNUPN.

24 Aug 2024, Gel status: 0

Created, Added New Source, Set mode of inheritance, Set publications, Set Phenotypes

Dmitrijs Rots (Children's Clinical University Hospital)

gene: SNUPN was added gene: SNUPN was added to Limb girdle muscular dystrophies, myofibrillar myopathies and distal myopathies. Sources: Literature Mode of inheritance for gene: SNUPN was set to BIALLELIC, autosomal or pseudoautosomal Publications for gene: SNUPN were set to 38413582 Phenotypes for gene: SNUPN were set to muscular dystrophy Review for gene: SNUPN was set to GREEN