Gene therapy clinical trials

Gene: WAS

Green List (high evidence)

WAS (Wiskott-Aldrich syndrome)
EnsemblGeneIds (GRCh38): ENSG00000015285
EnsemblGeneIds (GRCh37): ENSG00000015285
OMIM: 300392, Gene2Phenotype
WAS is in 10 panels

1 review

Ellen McDonagh (Genomics England Curator)

Green List (high evidence)

Genetic: Autologous CD34 positive cells transduced with a lentiviral vector containing human WAS gene - https://ClinicalTrials.gov/show/NCT01347242, Genetic: Autologous CD34+ cells transduced with WASP lentiviral vector - https://ClinicalTrials.gov/show/NCT02333760
Created: 12 May 2018, 8:57 a.m.

Phenotypes
Wiskott Aldrich syndrome

History Filter Activity

12 May 2018, Gel status: 4

Added New Source

Ellen McDonagh (Genomics England Curator)

WAS was added to Gene therapy clinical trials panel. Sources: ClinicalTrials.gov,Expert Review Green

12 May 2018, Gel status: 4

Created

Ellen McDonagh (Genomics England Curator)

WAS was created by Ellen McDonagh