Gene therapy clinical trialsGene: DMD
Drug: AVI-4658 (PMO) (intramuscular administered morpholino oligomer directed against exon 51) - trials https://ClinicalTrials.gov/show/NCT00159250 and https://clinicaltrials.gov/ct2/show/NCT00844597, Biological: BMS-986089|Biological: Placebo for BMS-986089 - https://ClinicalTrials.gov/show/NCT03039686
Created: 12 May 2018, 8:57 a.m.
Duchenne Muscular Dystrophy
Tag Skewed X-inactivation tag was added to gene: DMD.
DMD was added to Gene therapy clinical trials panel. Sources: ClinicalTrials.gov,Expert Review Green
DMD was created by Ellen McDonagh